FDA Denies Approval of Golodirsen for Duchenne Muscular Dystrophy
Golodirsen is a phosphorodiamidate morpholino oligomer.
Neurologic Disorders
Therapy That Targets Underlying Cause of Dravet Syndrome Gets Orphan Drug Status
The Food and Drug Administration has granted Orphan Drug designation to STK-001 (Stoke Therapeutics) for the treatment of Dravet syndrome.
FDA Clears Smartphone-Controlled Electroceutical for Acute Treatment of Migraine
The Food and Drug Administration (FDA) has cleared Nerivio Migra (Theranica), a prescription smartphone-controlled device for the acute treatment of migraine with or without aura in adults who do not have chronic migraine.
Microbial Growth Prompts Recall of Two Injectable Drugs
Heritage Pharmaceuticals has initiated a voluntary recall of Amikacin Sulfate Injection, USP, 1g/4mL (250mg/mL) and Prochlorperazine Edisylate Injection, USP, 10mg/2mL (5mg/mL) after microbial growth was detected in 1 unreleased sublot of both products.
FDA Warns Companies to Stop Selling Dietary Supplements That Claim to Treat Alzheimer Disease
These products may prevent patients from seeking appropriate treatment.
What Autism Can Teach Us About Brain Cancer
Applying lessons learned from autism to brain cancer, researchers at the Johns Hopkins University have discovered why elevated levels of the protein NHE9 add to the lethality of the most common and aggressive form of brain cancer, glioblastoma.
Scientists’ “Mad Cow” Discovery Points to Possible Neuron-Killing Mechanism Behind Alzheimer’s
Scientists from the Florida campus of The Scripps Research Institute (TSRI) have for the first time discovered a killing mechanism that could underpin a range of the most intractable neurodegenerative diseases, such as Alzheimers, Parkinsons, and ALS.
Researchers Make New Discoveries in Key Pathway for Neurological Diseases
A new intermediate step and unexpected enzymatic activity in a metabolic pathway in the body, which could lead to new drug design for psychiatric and neurodegenerative diseases, has been discovered by researchers at Georgia State University.
Epilepsy Research Opens a Window on the Brain
Rapidly emerging technologies, novel imaging techniques, and the development of new therapies and new genes have given researchers and clinicians an extraordinary ability to explore the brain at the cellular, genetic, and neural levels.
Alice in Wonderland Syndrome
Todds syndrome, more frequently referred to as Alice in Wonderland syndrome (AIWS), is a disorienting neurological condition that primarily targets children.
