First Ever Drug for Duchenne Muscular Dystrophy Approved by FDA
The FDA has just approved the drug, Exondys 51, to treat patients with a mutation of the dystrophin gene amenable to exon 51 skipping in DMD.
The FDA has just approved the drug, Exondys 51, to treat patients with a mutation of the dystrophin gene amenable to exon 51 skipping in DMD.