Sucraid Single-Use Containers Approved for Congenital Sucrase-Isomaltase Deficienc
Sucraid is an oral enzyme replacement therapy of the genetically determined sucrase deficiency.
Sucraid is an oral enzyme replacement therapy of the genetically determined sucrase deficiency.
The approval was based on data from the phase 3 TOPAZ-1 trial.
The treatment is expected to reprogram the immune system to induce tolerance to PDC-E2.
The approval was based on data from the phase 2b ICONIC study, along with 5 years of data from supportive studies.
Bylvay is an oral reversible inhibitor of the ileal bile acid transporter.
Devimistat targets the mitochondrial tricarboxylic acid cycle selectively in cancer cells.