HealthDay News — The US Food and Drug Administration has approved Emflaza (deflazacort) to treat Duchenne muscular dystrophy (DMD) in patients 5 years and older.

The corticosteroid is designed to reduce inflammation and suppress the immune system in patients with DMD, the most common type of muscular dystrophy. 

The FDA said it’s the first corticosteroid approved to treat DMD. Emflaza was evaluated in a clinical study of 196 males aged 5 to 15, all with documented mutation of the dystrophin gene and onset of DMD symptoms before age 5. 

Continue Reading

After 12 weeks, patients taking the drug showed muscle strength improvement, compared with those who took a placebo.

Side effects, similar to those caused by other corticosteroid medications, included facial puffiness, weight gain, increased appetite, upper respiratory tract infection, cough and increased need to urinate, the FDA said.

Emflaza is marketed by Marathon Pharmaceuticals, based in Northbrook, Illinois.


FDA Approves Drug to Treat Duchenne Muscular Dystrophy [press release]. Silver Spring, MD: US Food and Drug Administration; February 9, 2017.

Related Articles